Development and characterization of a first-in-class adjustable-dose gene therapy system

Alex Goraltchouk; Jared Lourie; Judith M. Hollander; H. Grace Rosen; Atsutaro A. Fujishiro; Francesco Luppino; Kai Zou; Alexey Seregin

doi:10.1016/j.gene.2024.148500

Development and characterization of a first-in-class adjustable-dose gene therapy system

Alex Goraltchouk
, Jared Lourie
, Judith M. Hollander
, H. Grace Rosen
, Atsutaro A. Fujishiro
, Francesco Luppino
, Kai Zou
, Alexey Seregin

Exercise & Health Science

Research output: Contribution to journal › Article › peer-review

Original language	English
Article number	148500
Journal	Gene
Volume	919
DOIs	https://doi.org/10.1016/j.gene.2024.148500
State	Published - Aug 15 2024

ASJC Scopus Subject Areas

Genetics

Keywords

Dose adjustment
Gene therapy
Lipid nanoparticles
Non-viral delivery
Subcutaneous

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10.1016/j.gene.2024.148500

Cite this

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title = "Development and characterization of a first-in-class adjustable-dose gene therapy system",

keywords = "Dose adjustment, Gene therapy, Lipid nanoparticles, Non-viral delivery, Subcutaneous",

author = "Alex Goraltchouk and Jared Lourie and Hollander, \{Judith M.\} and \{Grace Rosen\}, H. and Fujishiro, \{Atsutaro A.\} and Francesco Luppino and Kai Zou and Alexey Seregin",

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day = "15",

doi = "10.1016/j.gene.2024.148500",

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T1 - Development and characterization of a first-in-class adjustable-dose gene therapy system

AU - Goraltchouk, Alex

AU - Lourie, Jared

AU - Hollander, Judith M.

AU - Grace Rosen, H.

AU - Fujishiro, Atsutaro A.

AU - Luppino, Francesco

AU - Zou, Kai

AU - Seregin, Alexey

PY - 2024/8/15

Y1 - 2024/8/15

KW - Dose adjustment

KW - Gene therapy

KW - Lipid nanoparticles

KW - Non-viral delivery

KW - Subcutaneous

UR - https://www.scopus.com/pages/publications/85192059679

UR - https://www.scopus.com/pages/publications/85192059679#tab=citedBy

U2 - 10.1016/j.gene.2024.148500

DO - 10.1016/j.gene.2024.148500

M3 - Article

C2 - 38663689

AN - SCOPUS:85192059679

SN - 0378-1119

VL - 919

JO - Gene

JF - Gene

M1 - 148500

ER -

Development and characterization of a first-in-class adjustable-dose gene therapy system

ASJC Scopus Subject Areas

Keywords

Access to Document

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